Two compound heterozygous variants in the CLN8 gene are responsible for neuronal cereidolipofuscinoses disorder in a child: a case report

Background Neuronal Ceroid Lipofuscinosis (NCL) disorders, recognized as the primary cause of childhood dementia globally, constitute a spectrum of genetic abnormalities. CLN8, a subtype within NCL, is characterized by cognitive decline, motor impairment, and visual deterioration. This study focuses...

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Autore principale: Baltar, Federico (author)
Altri autori: Simoes, Camila (author), Garagorry, Francisco (author), Graña, Martín (author), Rodríguez, Soledad (author), Aunchayna, María Haydée (author), Tapié, Alejandra (author), Cerisola, Alfredo (author), González, Gabriel (author), Naya, Hugo (author), Spangenberg, Lucía (author), Raggio, Víctor (author)
Natura: article
Lingua:inglese
Pubblicazione: 2024
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Accesso online:https://hdl.handle.net/20.500.12381/4062
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